TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
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Descrição
Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.
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TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
Niemann–Pick disease, type C - Wikipedia
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